Tag: gene therapy

India getting close to developing gene therapy for sickle cell disease, say officials

June 19, 2024 admin

This microscope photo provided by the Centers for Disease Control and Prevention shows crescent-shaped red blood cells from a sickle cell disease patient. | Photo Credit: AP India is getting closer to developing a gene therapy for sickle cell disease, a genetic blood disorder with a high prevalence rate among the Scheduled Tribes, officials of…

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Gene therapy offers hope for patients with hearing loss

June 16, 2024 admin

Hearing loss is one of the most prevalent disorders and it is estimated that over one billion people suffer from hearing loss and approximately one-two children in every 1,000 births are born with congenital hearing loss. It is not therefore surprising that screening for newborns is an essential component of newborn screening programmes. Hearing loss…

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Pfizer reports patient death in Duchenne gene therapy study

May 8, 2024 admin

Pfizer’s gene therapy trial for Duchenne muscular dystrophy resulted in a young patient’s death. File | Photo Credit: Reuters A young patient died due to cardiac arrest after receiving Pfizer’s experimental gene therapy being tested in a mid-stage trial for a muscle-wasting disorder called Duchenne muscular dystrophy(DMD), the drugmaker told Reuters on May 7. “A…

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With CRISPR poised to revolutionise therapy, a pause to consider ethical issues

February 8, 2024 admin

“We will each write a ghost story”, said Lord Byron; and his proposition was acceded to. And so on a cold and rainy supposedly summer night in 1816, four friends inspired by German ghost stories, gathered to write one. Among them, a young Mary Shelley, consumed by the idea of creating a story that would “curdle…

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